Genetic disorders occur due to alterations in the primary genetic material—deoxyribonucleic acid (DNA)—of an organism.
CRISPR–Cas9-based therapies are widely investigated for their clinical applications. However, there are limitations ...
TEK IMAGE/Science Photo Library / Getty Images/Science Photo Libra A single infusion of an experimental gene-editing drug appears safe and effective for cutting cholesterol, possibly for life, ...
The need to change regulations around gene-editing treatments was endorsed in November by the head of the US Food and Drug ...
A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...
The Phase 1/2 trial is a first-in-human, open-label, multi-national study designed to evaluate the safety, tolerability, and efficacy of TSRA-196 in adults with AATD. Trial participants will receive a ...
A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new study, ...
A team of researchers at Columbia, Harvard and University of Minnesota has developed a gene editing technique they say could pave the way for new therapies for a host of diseases with fewer unintended ...
A single infusion of an experimental gene-editing drug appears safe and effective for cutting cholesterol, possibly for life, according to a small early study released Saturday. The study, which ...
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